ALNY
ALNYLAM PHARMACEUTICALS, INC.
Nasdaq: ALNY · Cambridge, MA · Healthcare
$308.43-2.51 (-0.81%)Closed
Market Cap$40.83B
Cash$1.66Bmost recent
Runway42 mo$118.3M Q burn
P/E (TTM)132.4EPS $2.33
52-Wk Range$236.75 – $491.22
Avg Volume1.2M3-month
Price & Trading Activity

Daily close with catalyst overlays and trading volume

$308.43+111.6%
Pipeline

Drug candidates sponsored by ALNYLAM PHARMACEUTICALS · ClinicalTrials.gov

52 drugs · 80 trials
PhaseDrug / CandidateIndicationsStatusNext CompletionTrials
Phase 3Revusiran (ALN-TTRSC)
Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)+6 more
Completed
2017-03-30past
2
Phase 3patisiran (ALN-TTR02)
TTR-mediated Amyloidosis+6 more
Completed
2017-08past
3
Phase 3Givosiran
Acute Hepatic Porphyria+8 more
Completed
2021-11-05past
4
Phase 3Patisiran
Amyloidosis, Familial+8 more
Completed
2022-11-23past
6
Phase 3Lumasiran
Primary Hyperoxaluria+8 more
Completed
2023-02-07past
6
Phase 3Placebo
Primary Hyperoxaluria Type 1 (PH1)+6 more
Recruiting
2027-08-09
5
Phase 3Nucresiran
Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy+2 more
Recruiting
2027-12-27
2
Phase 3Vutrisiran
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Active, not recruiting
2028-03-31
2
Phase 3Zilebesiran
High Risk Cardiovascular Disease+3 more
Recruiting
2030-09-30
3
Phase 2ALN-RSV01
Respiratory Syncytial Virus Infections
Completed
2012-04past
3
Phase 2ALN-TTRSC (revusiran) for subcutaneous administration
TTR-mediated Amyloidosis
Completed
2014-10past
1
Phase 1ALN-CC5
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Completed
2016-04past
1
Phase 2ALN-TTR02 (patisiran) administered by intravenous (IV) infusion
TTR-mediated Amyloidosis
Completed
2016-07past
1
Phase 2Revusiran
Transthyretin (TTR)-Mediated Amyloidosis+3 more
Completed
2017-02-06past
1
Phase 2Cemdisiran
Atypical Hemolytic Uremic Syndrome
Withdrawn
2018-09-12past
1
Phase 1ALN-AAT02
ZZ Type Alpha-1 Antitrypsin Deficiency Liver Disease
Terminated
2020-06-25past
1
Phase 1ALN-XDH
Gout
Terminated
2023-01-25past
1
Phase 2Indapamide
Hypertension
Completed
2023-12-11past
1
Phase 1ALN-KHK
Type 2 Diabetes Mellitus (T2DM)
Terminated
2025-04-03past
1
Phase 2ALN-4324
Type 2 Diabetes Mellitus (T2DM)+1 more
Recruiting
2027-05-28
2
Phase 1ALN-6400
Hereditary Hemorrhagic Telangiectasia
Recruiting
2028-01-05
1
Phase 1ALN-2232
Obesity
Recruiting
2028-02-01
1
Phase 1ALN-TTR01
Transthyretin Mediated Amyloidosis (ATTR)
Completed
2012-01past
1
Phase 1ALN-PCS02
Elevated LDL-Cholesterol (LDL-C)
Completed
2012-03past
1
Phase 1ALN-TTR02
TTR-mediated Amyloidosis
Completed
2012-06past
1
Phase 1ALN-VSP02
Solid Tumors
Completed
2012-08past
2
Phase 1ALN-TTRSC (revusiran)
TTR-mediated Amyloidosis
Completed
2015-04past
1
Phase 1ALN-PCSSC
Hypercholesterolemia
Completed
2015-05past
1
Phase 1givosiran (ALN-AS1)
Acute Intermittent Porphyria
Completed
2017-09-06past
1
Phase 1ALN-HBV
Hepatitis B+4 more
Terminated
2017-10past
1
Phase 1ALN-AAT
Antitrypsin Deficiency Liver Disease
Terminated
2018-01-03past
1
Phase 1ALN-TTRSC02
Transthyretin-mediated Amyloidosis (ATTR Amyloidosis)
Completed
2018-01-12past
1
Phase 1ALN-AGT01
Hypertension
Completed
2022-04-20past
1
Phase 1ALN-HSD
Nonalcoholic Steatohepatitis+1 more
Terminated
2023-01-06past
1
Phase 1ALN-AGT01 RVR
Healthy Volunteers
Completed
2025-09-08past
1
Phase 1ALN-TTRSC04
Transthyretin-Mediated Amyloidosis
Completed
2025-09-30past
1
Phase 1ALN-4285
Healthy Volunteers
Recruiting
2026-12-29
1
Phase 1ALN-4915
Healthy Volunteers
Recruiting
2027-07-31
1
Phase 1ALN-BCAT
Advanced Hepatocellular Carcinoma+1 more
Recruiting
2027-09-30
1
Phase 1ALN-HTT02
Huntington's Disease
Recruiting
2028-07-05
1
Phase 1ALN-APP
Early-Onset Alzheimer Disease
Recruiting
2029-04-20
1
Phase 1ALN-5288
Alzheimer's Disease
Recruiting
2030-03-06
1
N/AUnnamed
Familial Amyloidotic Cardiomyopathy (FAC)
Completed
2016-01past
1
N/AUnnamed
Acute Hepatic Porphyria+6 more
Terminated
2019-01-15past
1
N/AUnnamed
Amyloidosis+1 more
Terminated
2020-05-18past
1
N/AUnnamed
Acute Hepatic Porphyria
Completed
2021-04-26past
1
N/AUnnamed
Acute Hepatic Porphyria
Recruiting
2027-04-01
1
N/AUnnamed
Hereditary Amyloidosis, Transthyretin-Related+1 more
Recruiting
2027-12-01
1
N/AUnnamed
Primary Hyperoxaluria Type 1
Active, not recruiting
2028-09-01
1
N/AUnnamed
Transthyretin-Mediated Amyloidosis+1 more
Recruiting
2030-09-01
1
N/AUnnamed
Hereditary Transthyretin-mediated (hATTR) Amyloidosis+1 more
Recruiting
2030-10-12
1
N/AUnnamed
Transthyretin Amyloidosis With Cardiomyopathy
Recruiting
2030-10-23
1
Valuation

Risk-adjusted NPV

Loading pipeline…
Peer comparison

Cohort check

No peer cohort defined for ALNY. Cohorts currently cover gene editing, mRNA, rare-disease gene therapy, and large-cap biotech — more coming soon.