PTCT
PTC THERAPEUTICS, INC.
Nasdaq: PTCT · Warren, NJ · Healthcare
$70.63-1.69 (-2.34%)Closed
Market Cap$5.75B
Cash$1.95Bmost recent
Runwayprofitable
P/E (TTM)9.1EPS $7.78
52-Wk Range$36.19 – $86.25
Avg Volume1.3M3-month
Price & Trading Activity
Daily close with catalyst overlays and trading volume
$70.63+172.0%
Pipeline
Drug candidates sponsored by PTC THERAPEUTICS · ClinicalTrials.gov
| Phase | Drug / Candidate | Indications | Status | Next Completion | Trials | |
|---|---|---|---|---|---|---|
| Phase 3 | Ataluren (PTC124®) | Cystic Fibrosis | Completed | 2016-11past | 1 | |
| Phase 3 | Deflazacort | Limb-Girdle Muscular Dystrophy+4 more | Completed | 2021-07-31past | 8 | |
| Phase 2 | PTC299 | Pneumonia+7 more | Completed | 2022-07-20past | 5 | |
| Phase 2 | Unesbulin | Leiomyosarcoma | Completed | 2024-06-17past | 2 | |
| Phase 3 | Ataluren | Cystic Fibrosis+19 more | Completed | 2026-02-10past | 24 | |
| Phase 3 | PTC923 | Phenylketonuria+2 more | Active, not recruiting | 2026-06-30 | 3 | |
| Phase 2 | Vatiquinone | Mitochondrial Diseases+9 more | Active, not recruiting | 2027-12-31 | 5 | |
| Phase 3 | Sepiapterin | Phenylketonuria | Recruiting | 2031-02-28 | 1 | |
| Phase 2 | PTC124 | Cystic Fibrosis+1 more | Completed | 2007-07past | 3 | |
| Phase 2 | Placebo | Leigh Syndrome+1 more | Completed | 2015-10-31past | 2 | |
| Phase 2 | EPI-589 | Amyotrophic Lateral Sclerosis | Completed | 2018-02-23past | 1 | |
| Phase 2 | CNSA-001 | Gastroparesis | Completed | 2019-09-08past | 1 | |
| Phase 2 | Eladocagene Exuparvovec | AADC Deficiency | Active, not recruiting | 2023-05-22past | 1 | |
| Phase 2 | EPI-743 | Leigh Syndrome+1 more | Completed | 2023-10-30past | 2 | |
| Phase 2 | PTC857 | Amyotrophic Lateral Sclerosis | Terminated | 2024-09-26past | 1 | |
| Phase 2 | PTC518 | Huntington Disease | Completed | 2025-02-07past | 1 | |
| Phase 1 | Deflazacort and rifampin | Healthy Volunteers | Completed | 2014-12past | 1 | |
| Phase 1 | PTC596 | Cancer | Completed | 2017-02-06past | 1 | |
| N/A | Unnamed | Muscular Dystrophy, Duchenne | Completed | 2025-03-31past | 1 |
Valuation
Risk-adjusted NPV
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Peer comparison
Cohort check
No peer cohort defined for PTCT. Cohorts currently cover gene editing, mRNA, rare-disease gene therapy, and large-cap biotech — more coming soon.